Research Summary
Orphan drugs, also known as orphan medicinal products, are pharmaceutical substances developed to diagnose, prevent, or treat rare diseases and conditions that affect a small percentage of the population. These diseases, often referred to as orphan diseases, are typically life-threatening or chronically debilitating and can be genetic, infectious, or autoimmune in nature. Due to the limited prevalence of these conditions, traditional pharmaceutical companies may have little incentive to invest in developing treatments. Orphan drug status is granted by regulatory agencies to incentivize pharmaceutical companies to research and develop therapies for these rare diseases. This designation may include benefits such as extended market exclusivity, tax incentives, and reduced regulatory requirements, encouraging the development of drugs that might otherwise not be economically viable. Orphan drugs have played a significant role in improving the quality of life and life expectancy of individuals with rare diseases.
According to DIResearch's in-depth investigation and research, the global Orphan Drugs market size will reach US$ XX Million in 2024, and is expected to reach US$ XX Million in 2030, with a CAGR of XX% (2025-2030). Among them, the China market has changed rapidly in the past few years. The market size in 2024 will be US$ XX Million, accounting for approximately XX% of the world. It is expected to reach US$ XX Million in 2030, and the global share will reach XX%.
The major global manufacturers of Orphan Drugs include Bristol-Myers Squibb, Roche, Novartis, Johnson & Johnson, Pfizer, Amgen, Sanofi, AstraZeneca, Takeda, Vertex Pharmaceuticals, AbbVie, Biogen, Eli Lilly etc. The global players competition landscape in this report is divided into three tiers. The first tiers is the global leading enterprise, which occupies a major market share, is in a leading position in the industry, has strong competitiveness and influence, and has a large revenue scale; the second tiers has a certain share and popularity in the market, actively follows the industry leaders in product, service or technological innovation, and has a medium revenue scale; the third tiers has a smaller share in the market, has a lower brand awareness, mainly focuses on the local market, and has a relatively small revenue scale.
This report studies the market size, price trends and future development prospects of Orphan Drugs. Focus on analysing the market share, product portfolio, revenue and gross profit margin of global major manufacturers, as well as the market status and trends of different product types and applications in the global Orphan Drugs market. The report data covers historical data from 2019 to 2023, base year in 2024 and forecast data from 2025 to 2030.
The regions and countries in the report include North America, Europe, China, APAC (excl. China), Latin America and Middle East and Africa, covering the Orphan Drugs market conditions and future development trends of key regions and countries, combined with industry-related policies and the latest technological developments, analyze the development characteristics of Orphan Drugs industries in various regions and countries, help companies understand the development characteristics of each region, help companies formulate business strategies, and achieve the ultimate goal of the company's global development strategy.
The data sources of this report mainly include the National Bureau of Statistics, customs databases, industry associations, corporate financial reports, third-party databases, etc. Among them, macroeconomic data mainly comes from the National Bureau of Statistics, International Economic Research Organization; industry statistical data mainly come from industry associations; company data mainly comes from interviews, public information collection, third-party reliable databases, and price data mainly comes from various markets monitoring database.
Global Key Manufacturers of Orphan Drugs Include:
Bristol-Myers Squibb
Roche
Novartis
Johnson & Johnson
Pfizer
Amgen
Sanofi
AstraZeneca
Takeda
Vertex Pharmaceuticals
AbbVie
Biogen
Eli Lilly
Orphan Drugs Product Segment Include:
Oncology
Pulmonary
Neurology
Hematology
Endocrinology
Cardio-vascular
Metabolic Disorders
Others
Orphan Drugs Product Application Include:
Baby and Child
Teenager
Adult
Others
Chapter Scope
Chapter 1: Product Research Range, Product Types and Applications, Market Overview, Market Situation and Trends
Chapter 2: Global Orphan Drugs Industry PESTEL Analysis
Chapter 3: Global Orphan Drugs Industry Porter's Five Forces Analysis
Chapter 4: Global Orphan Drugs Major Regional Market Size and Forecast Analysis
Chapter 5: Global Orphan Drugs Market Size and Forecast by Type and Application Analysis
Chapter 6: North America Orphan Drugs Competitive Analysis (Market Size, Key Players and Market Share, Product Type and Application Segment Analysis, Countries Analysis)
Chapter 7: Europe Orphan Drugs Competitive Analysis (Market Size, Key Players and Market Share, Product Type and Application Segment Analysis, Countries Analysis)
Chapter 8: China Orphan Drugs Competitive Analysis (Market Size, Key Players and Market Share, Product Type and Application Segment Analysis, Countries Analysis)
Chapter 9: APAC (Excl. China) Orphan Drugs Competitive Analysis (Market Size, Key Players and Market Share, Product Type and Application Segment Analysis, Countries Analysis)
Chapter 10: Latin America Orphan Drugs Competitive Analysis (Market Size, Key Players and Market Share, Product Type and Application Segment Analysis, Countries Analysis)
Chapter 11: Middle East and Africa Orphan Drugs Competitive Analysis (Market Size, Key Players and Market Share, Product Type and Application Segment Analysis, Countries Analysis)
Chapter 12: Global Orphan Drugs Competitive Analysis of Key Manufacturers (Revenue, Market Share, Regional Distribution and Industry Concentration)
Chapter 13: Key Company Profiles (Product Portfolio, Revenue and Gross Margin)
Chapter 14: Industrial Chain Analysis, Include Raw Material Suppliers, Distributors and Customers
Chapter 15: Research Findings and Conclusion
Chapter 16: Methodology and Data Sources
Table of Contents 1 Orphan Drugs Market Overview 1.1 Product Definition and Statistical Scope 1.2 Orphan Drugs Product by Type 1.2.1 Global Orphan Drugs Market Size by Type, 2023 VS 2024 VS 2030 1.2.2 Oncology 1.2.3 Pulmonary 1.2.4 Neurology 1.2.5 Hematology 1.2.6 Endocrinology 1.2.7 Cardio-vascular 1.2.8 Metabolic Disorders 1.2.9 Others 1.3 Orphan Drugs Product by Application 1.3.1 Global Orphan Drugs Market Size by Application, 2023 VS 2024 VS 2030 1.3.2 Baby and Child 1.3.3 Teenager 1.3.4 Adult 1.3.5 Others 1.4 Global Orphan Drugs Market Revenue Analysis (2019-2030) 1.5 Orphan Drugs Market Development Status and Trends 1.5.1 Orphan Drugs Industry Development Status Analysis 1.5.2 Orphan Drugs Industry Development Trends Analysis 2 Orphan Drugs Market PESTEL Analysis 2.1 Political Factors Analysis 2.2 Economic Factors Analysis 2.3 Social Factors Analysis 2.4 Technological Factors Analysis 2.5 Environmental Factors Analysis 2.6 Legal Factors Analysis 3 Orphan Drugs Market Porter's Five Forces Analysis 3.1 Competitive Rivalry 3.2 Threat of New Entrants 3.3 Bargaining Power of Suppliers 3.4 Bargaining Power of Buyers 3.5 Threat of Substitutes 4 Global Orphan Drugs Market Analysis by Regions 4.1 Orphan Drugs Overall Market: 2023 VS 2024 VS 2030 4.2 Global Orphan Drugs Revenue and Forecast Analysis (2019-2030) 4.2.1 Global Orphan Drugs Revenue and Market Share by Region (2019-2024) 4.2.2 Global Orphan Drugs Revenue Forecast by Region (2025-2030) 5 Global Orphan Drugs Market Size by Type and Application 5.1 Global Orphan Drugs Market Size by Type 5.2 Global Orphan Drugs Market Size by Application 6 North America 6.1 North America Orphan Drugs Market Size and Growth Rate Analysis (2019-2030) 6.2 North America Key Manufacturers Analysis 6.3 North America Orphan Drugs Market Size by Type 6.4 North America Orphan Drugs Market Size by Application 6.5 North America Orphan Drugs Market Size by Country 6.5.1 US 6.5.2 Canada 7 Europe 7.1 Europe Orphan Drugs Market Size and Growth Rate Analysis (2019-2030) 7.2 Europe Key Manufacturers Analysis 7.3 Europe Orphan Drugs Market Size by Type 7.4 Europe Orphan Drugs Market Size by Application 7.5 Europe Orphan Drugs Market Size by Country 7.5.1 Germany 7.5.2 France 7.5.3 United Kingdom 7.5.4 Italy 7.5.5 Spain 7.5.6 Benelux 8 China 8.1 China Orphan Drugs Market Size and Growth Rate Analysis (2019-2030) 8.2 China Key Manufacturers Analysis 8.3 China Orphan Drugs Market Size by Type 8.4 China Orphan Drugs Market Size by Application 9 APAC (excl. China) 9.1 APAC (excl. China) Orphan Drugs Market Size and Growth Rate Analysis (2019-2030) 9.2 APAC (excl. China) Key Manufacturers Analysis 9.3 APAC (excl. China) Orphan Drugs Market Size by Type 9.4 APAC (excl. China) Orphan Drugs Market Size by Application 9.5 APAC (excl. China) Orphan Drugs Market Size by Country 9.5.1 Japan 9.5.2 South Korea 9.5.3 India 9.5.4 Australia 9.5.5 Indonesia 9.5.6 Vietnam 9.5.7 Malaysia 9.5.8 Thailand 10 Latin America 10.1 Latin America Orphan Drugs Market Size and Growth Rate Analysis (2019-2030) 10.2 Latin America Key Manufacturers Analysis 10.3 Latin America Orphan Drugs Market Size by Type 10.4 Latin America Orphan Drugs Market Size by Application 10.5 Latin America Orphan Drugs Market Size by Country 10.5.1 Mecixo 10.5.2 Brazil 11 Middle East & Africa 11.1 Middle East & Africa Orphan Drugs Market Size and Growth Rate Analysis (2019-2030) 11.2 Middle East & Africa Key Manufacturers Analysis 11.3 Middle East & Africa Orphan Drugs Market Size by Type 11.4 Middle East & Africa Orphan Drugs Market Size by Application 11.5 Middle East & Africa Orphan Drugs Market Size by Country 11.5.1 Saudi Arabia 11.5.2 South Africa 12 Market Competition by Manufacturers 12.1 Global Orphan Drugs Market Revenue by Key Manufacturers (2020-2024) 12.2 Orphan Drugs Competitive Landscape Analysis and Market Dynamic 12.2.1 Orphan Drugs Competitive Landscape Analysis 12.2.2 Global Key Manufacturers Headquarter and Key Area Sales 12.2.3 Market Dynamic 13 Key Companies Analysis 13.1 Bristol-Myers Squibb 13.1.1 Bristol-Myers Squibb Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.1.2 Bristol-Myers Squibb Orphan Drugs Product Portfolio 13.1.3 Bristol-Myers Squibb Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.2 Roche 13.2.1 Roche Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.2.2 Roche Orphan Drugs Product Portfolio 13.2.3 Roche Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.3 Novartis 13.3.1 Novartis Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.3.2 Novartis Orphan Drugs Product Portfolio 13.3.3 Novartis Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.4 Johnson & Johnson 13.4.1 Johnson & Johnson Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.4.2 Johnson & Johnson Orphan Drugs Product Portfolio 13.4.3 Johnson & Johnson Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.5 Pfizer 13.5.1 Pfizer Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.5.2 Pfizer Orphan Drugs Product Portfolio 13.5.3 Pfizer Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.6 Amgen 13.6.1 Amgen Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.6.2 Amgen Orphan Drugs Product Portfolio 13.6.3 Amgen Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.7 Sanofi 13.7.1 Sanofi Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.7.2 Sanofi Orphan Drugs Product Portfolio 13.7.3 Sanofi Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.8 AstraZeneca 13.8.1 AstraZeneca Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.8.2 AstraZeneca Orphan Drugs Product Portfolio 13.8.3 AstraZeneca Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.9 Takeda 13.9.1 Takeda Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.9.2 Takeda Orphan Drugs Product Portfolio 13.9.3 Takeda Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.10 Vertex Pharmaceuticals 13.10.1 Vertex Pharmaceuticals Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.10.2 Vertex Pharmaceuticals Orphan Drugs Product Portfolio 13.10.3 Vertex Pharmaceuticals Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.11 AbbVie 13.11.1 AbbVie Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.11.2 AbbVie Orphan Drugs Product Portfolio 13.11.3 AbbVie Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.12 Biogen 13.12.1 Biogen Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.12.2 Biogen Orphan Drugs Product Portfolio 13.12.3 Biogen Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 13.13 Eli Lilly 13.13.1 Eli Lilly Basic Company Profile (Employees, Areas Service, Competitors and Contact Information) 13.13.2 Eli Lilly Orphan Drugs Product Portfolio 13.13.3 Eli Lilly Orphan Drugs Market Data Analysis (Revenue, Gross Margin and Market Share) (2020-2024) 14 Industry Chain Analysis 14.1 Orphan Drugs Industry Chain Analysis 14.2 Orphan Drugs Industry Raw Material and Suppliers Analysis 14.2.1 Upstream Key Raw Material Supply Analysis 14.2.2 Raw Material Suppliers and Contact Information 14.3 Orphan Drugs Typical Downstream Customers 14.4 Orphan Drugs Sales Channel Analysis 15 Research Findings and Conclusion 16 Methodology and Data Source 16.1 Methodology/Research Approach 16.2 Research Scope 16.3 Benchmarks and Assumptions 16.4 Date Source 16.4.1 Primary Sources 16.4.2 Secondary Sources 16.5 Data Cross Validation 16.6 Disclaimer
Publisher: DIResearch
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